We aim to develop innovative, RNA-based therapeutics to fill unmet medical needs for patients with genetic diseases
Duchenne Muscular Dystrophy Patient Stories
Janneke, mother of Jayden
"I don’t want to raise him in an overly protective environment."
Johny & Wanda, parents of Stan
"When will the doctors find a pill for my sick muscles? I want to be able to jump again."
Jo & Ilse, parents of Maarten
"At school, they would do anything for him. All of the children in his class are his personal bodyguards."
Teun & Esther, parents of Thomas
"DMD immediately makes you once again realise what is and isn’t important in life."
Dree & Margot, parents of Bram
"Mum, will I ever ride without training wheels?"
Latest Press Releases
May. 28, 2013
Feb. 27, 2013
Feb. 7, 2013
Jan. 29, 2013