We aim to develop innovative, RNA-based therapeutics to address unmet medical needs for patients with genetic disorders.
Duchenne Muscular Dystrophy Patient Stories
Janneke, mother of Jayden
"I don’t want to raise him in an overly protective environment."
Johny & Wanda, parents of Stan
"When will the doctors find a pill for my sick muscles? I want to be able to jump again."
Jo & Ilse, parents of Maarten
"At school, they would do anything for him. All of the children in his class are his personal bodyguards."
Teun & Esther, parents of Thomas
"DMD immediately makes you once again realise what is and isn’t important in life."
Dree & Margot, parents of Bram
"Mum, will I ever ride without training wheels?"