Technology & Products
RNA Modulation
Our RNA-modulating therapeutics aim at targeted modulation of gene expression employing single-stranded RNA-based antisense oligonucleotides (AONs).
Exon Skipping
Our exon skipping technology is based on interference with exon inclusion signals during the splicing of the pre-mRNA, in order to induce the skipping of the targeted exon from the mature mRNA (messenger RNA) and to increase the level of functional transcripts.
IP Portfolio
Prosensa has ensured strong IP protection for its lead products in DMD in both Europe and the US. In addition, Prosensa has developed or licensed a broad set of patent families covering pipeline products and discovery projects.